Program Details
Applicant Information
Applicant Name
*
First Name
Last Name
Applicant Email
*
example@example.com
Applicant Institution
*
Applicant Position
*
Undergraduate Researcher
Graduate Researcher
Postdoctorate Researcher
Principal Investigator
Other
Please specify your position
Principal Investigator (PI) Information
PI Name
*
First Name
Last Name
PI Email
*
example@example.com
Technology Transfer Office (TTO) Contact
TTO Contact Name
*
First Name
Last Name
TTO Contact Email
*
example@example.com
Research / Development Information
Number of Indications / Programs
*
1
2
3
4
5
Number of Indications / Programs
*
Please Select
1
2
3
4
5
Indication / Program (1)
Disease Indication (1)
*
Capsids Used (1)
*
e.g., AAV9, AAV PHP.eB, engineered variants.
Development Stage (1)
*
Include high level overview of partial or completed in vitro and/or in vivo studies and payload design status.
Development Plan (1)
*
In a high level summary, describe intended research plan utilizing TfR1 CapX.
Next Anticipated Regulatory Meeting Type (1)
None anticipated
FDA - INTERACT
FDA - Pre-IND
FDA - IND
FDA - Type D Meeting
Unsure – Need Advice
Other
Please Specify The Meeting Type (1)
Meeting Month (1)
Please Select
January
February
March
April
May
June
July
August
September
October
November
December
Meeting Year (1)
Please Select
2025
2026
2027
2028
2029
2030
Indication / Program (2)
Disease Indication (2)
*
Capsids Used (2)
*
e.g., AAV9, AAV PHP.eB, engineered variants.
Development Stage (2)
*
Include high level overview of partial or completed in vitro and/or in vivo studies and payload design status.
Development Plan (2)
*
In a high level summary, describe intended research plan utilizing TfR1 CapX.
Next Anticipated Regulatory Meeting Type (2)
None anticipated
FDA - INTERACT
FDA - Pre-IND
FDA - IND
FDA - Type D Meeting
Unsure – Need Advice
Other
Please Specify The Meeting Type (2)
Meeting Month (2)
Please Select
January
February
March
April
May
June
July
August
September
October
November
December
Meeting Year (2)
Please Select
2025
2026
2027
2028
2029
2030
Indication / Program (3)
Disease Indication (3)
*
Capsids Used (3)
*
e.g., AAV9, AAV PHP.eB, engineered variants.
Development Stage (3)
*
Include high level overview of partial or completed in vitro and/or in vivo studies and payload design status.
Development Plan (3)
*
In a high level summary, describe intended research plan utilizing TfR1 CapX.
Next Anticipated Regulatory Meeting Type (3)
None anticipated
FDA - INTERACT
FDA - Pre-IND
FDA - IND
FDA - Type D Meeting
Unsure – Need Advice
Other
Please Specify The Meeting Type (3)
Meeting Month (3)
Please Select
January
February
March
April
May
June
July
August
September
October
November
December
Meeting Year (3)
Please Select
2025
2026
2027
2028
2029
2030
Indication / Program (4)
Disease Indication (4)
*
Capsids Used (4)
*
e.g., AAV9, AAV PHP.eB, engineered variants.
Development Stage (4)
*
Include high level overview of partial or completed in vitro and/or in vivo studies and payload design status.
Development Plan (4)
*
In a high level summary, describe intended research plan utilizing TfR1 CapX.
Next Anticipated Regulatory Meeting Type (4)
None anticipated
FDA - INTERACT
FDA - Pre-IND
FDA - IND
FDA - Type D Meeting
Unsure – Need Advice
Other
Please Specify The Meeting Type (4)
Meeting Month (4)
Please Select
January
February
March
April
May
June
July
August
September
October
November
December
Meeting Year (4)
Please Select
2025
2026
2027
2028
2029
2030
Indication / Program (5)
Disease Indication (5)
*
Capsids Used (5)
*
e.g., AAV9, AAV PHP.eB, engineered variants.
Development Stage (5)
*
Include high level overview of partial or completed in vitro and/or in vivo studies and payload design status.
Development Plan (5)
*
In a high level summary, describe intended research plan utilizing TfR1 CapX.
Next Anticipated Regulatory Meeting Type (5)
None anticipated
FDA - INTERACT
FDA - Pre-IND
FDA - IND
FDA - Type D Meeting
Unsure – Need Advice
Other
Please Specify The Meeting Type (5)
Meeting Month (5)
Please Select
January
February
March
April
May
June
July
August
September
October
November
December
Meeting Year (5)
Please Select
2025
2026
2027
2028
2029
2030
Save & Submit
Submit
Should be Empty: